Medical Science Liaison - Rare Diseases & KOL Expert

PTC Therapeutics, Inc

Philadelphia (Philadelphia County)

On-site

USD 153,000 - 199,000

Full time

14 days+

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Job summary

PTC Therapeutics, Inc is seeking a Medical Science Liaison (MSL) to work in the field, engaging with KOLs, clinicians, academic centers, and payors to discuss PTC products and disease states. You will build long-term relationships through scientific discussions and ensure proper product utilization.

The role requires advanced scientific credentials and at least 2 years of MSL experience, with travel up to 50–60%.

Qualifications

  • Advanced scientific degree and minimum 2 years as MSL.
  • Experience with orphan/rare diseases.
  • Experience with high-cost specialty products and patient access coordination.
  • Proven ability to work with KOLs, clinicians, payors and academia.
  • Excellent scientific/technical writing and presentations.

Responsibilities

  • Attend national and regional meetings and symposia; gather and summarize information; cultivate relationships.
  • Deliver fair, objective clinical presentations to HCPs, payors and patient orgs.
  • Identify speakers for advisory boards and educational programs.
  • Support regional medical initiatives and advisory boards.
  • Provide input to management on competitive therapies, BD opportunities/risks, and market insights.
  • Establish and maintain relationships with health authorities, HCPs, payors, and academia.
  • Submit unrestricted educational grants or research initiative requests per policy.
  • Maintain awareness of regulatory, compliance, quality issues relevant to PTC areas.
  • Monitor competitive therapies and communicate data succinctly to stakeholders.

Skills

Verbal & written comms
Influence without authority
Analytical thinking

Education

Advanced scientific degree (PhD, PharmD, MD, DNP, MSN, MS, Registered Dietician, or Genetic Counselor)
2+ years MSL experience

Tools

Microsoft Office

Job description

PTC Therapeutics, Inc is seeking a Medical Science Liaison (MSL) to work in the field, engaging with KOLs, clinicians, academic centers, and payors to discuss PTC products and disease states. You will build long-term relationships through scientific discussions and ensure proper product utilization.

The role requires advanced scientific credentials and at least 2 years of MSL experience, with travel up to 50–60%.

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Incentives (short- & long-term)
Benefits: medical, dental, vision, 401