Field-Based Medical Science Liaison — Rare Diseases

PTC Therapeutics, Inc

Charleston (WV)

On-site

USD 153,000 - 199,000

Full time

7 days ago
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Job summary

PTC Therapeutics, Inc. is seeking a Medical Science Liaison (MSL) to represent our products to KOLs, clinicians, and academic centers.

The MSL will build long-term scientific relationships through high-level disease-state discussions, support market insights, and align cross-functional teams in Medical Affairs. The role requires advanced scientific credentials with at least 2 years as an MSL, experience with orphan/rare diseases, and the ability to travel 50–60% in a field-based capacity.

Qualifications

  • Advanced degree in life sciences with at least 2 years as MSL.
  • Experience supporting orphan/rare diseases, preferably PKU.
  • Experience coordinating with patient access for high-cost therapies.
  • Proven ability to build and maintain relationships with KOLs, clinicians, payors.
  • Excellent written and verbal communication of complex scientific data.
  • Willingness to travel 50–60% and work independently.

Responsibilities

  • Attend national and regional medical meetings and represent PTC.
  • Deliver fair-balanced clinical presentations to HCPs, payors, patient groups.
  • Identify speakers for advisory boards and educational programs.
  • Support regional medical initiatives and provide market insights.
  • Collaborate with internal/external teams in Medical Affairs.
  • Ensure compliance with SOPs, regulatory requirements and credentialing.
  • Maintain relations with health authorities and academic institutions.

Skills

KOL relationships
Scientific communication
Independent / team work
Travel readiness

Education

Advanced life sciences degree

Tools

Microsoft Office

Job description

PTC Therapeutics, Inc. is seeking a Medical Science Liaison (MSL) to represent our products to KOLs, clinicians, and academic centers.

The MSL will build long-term scientific relationships through high-level disease-state discussions, support market insights, and align cross-functional teams in Medical Affairs. The role requires advanced scientific credentials with at least 2 years as an MSL, experience with orphan/rare diseases, and the ability to travel 50–60% in a field-based capacity.

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