Field-Based Medical Science Liaison: Rare Diseases

PTC Therapeutics, Inc

West Virginia

On-site

USD 153,000 - 199,000

Full time

8 days ago
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Job summary

PTC Therapeutics, Inc. is seeking a Medical Science Liaison (MSL) to engage with KOLs, clinicians, and academic institutions across our rare-disease portfolio.

This field-based role requires scientific excellence, strategic communication, and cross-functional collaboration to support product knowledge and medical initiatives. The MSL will travel 50–60% of the time, build trusted relationships, deliver balanced scientific presentations, and partner with Medical Affairs to advance education and

Qualifications

  • Advanced scientific degree with a minimum of 2 years as Medical Science Liaison
  • Experience with orphan products, rare diseases, genetics or Inborn Errors of Metabolism preferred
  • Proven ability to engage KOLs, clinicians, payors and academic institutions
  • Excellent written and verbal communication; ability to present complex data clearly

Responsibilities

  • Attend national and regional medical meetings as a representative and summarize findings
  • Deliver fair-balanced clinical presentations to healthcare professionals and patient organizations
  • Identify speakers for advisory boards, symposia, and educational programs
  • Support regional medical initiatives and provide market insights to management
  • Establish and maintain relations with health authorities, KOLs, HCPs, payors and patient organizations
  • Submit educational grants or research initiatives per company policy
  • Maintain awareness of medical, regulatory and quality issues in therapeutic areas
  • Monitor competitor information and communicate insights to internal stakeholders

Skills

KOL engagement
Scientific communication
Cross-functional collaboration
Travel readiness
Microsoft Office

Education

PhD/PharmD/MD/etc.

Tools

Microsoft Office

Job description

PTC Therapeutics, Inc. is seeking a Medical Science Liaison (MSL) to engage with KOLs, clinicians, and academic institutions across our rare-disease portfolio.

This field-based role requires scientific excellence, strategic communication, and cross-functional collaboration to support product knowledge and medical initiatives. The MSL will travel 50–60% of the time, build trusted relationships, deliver balanced scientific presentations, and partner with Medical Affairs to advance education and

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